Koch, Peter J.Koster, Maranke I.2022-08-052022-08-052021-08-061664-8021http://hdl.handle.net/10342/10980en-USectodermal dysplasiarare genetic disordersgene therapyRare Genetic Disorders: Novel Treatment Strategies and Insights Into Human BiologyArticle10.3389/fgene.2021.714764